Publications

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Blindness
TitleAuthorsPublication Year
High-efficiency base editing in the retina in primates and human tissues Alissa Muller, Jack Sullivan, Wibke Schwarzer, Mantian Wang, Cindy Park-Windhol, Pascal W Hasler, Lucas Janeschitz-Kriegl, Mert Duman, Beryll Klingler, Jane Matsell, Simon Manuel Hostettler, Patricia Galliker, Yanyan Hou, Pierre Balmer, Tamás Virág, Luis Alberto Barrera, Lauren Young, Quan Xu, Dániel Péter Magda, Ferenc Kilin, Arogya Khadka, Pierre-Henri Moreau, Lyne Fellmann, Thierry Azoulay, Mathieu Quinodoz, Duygu Karademir, Juna Leppert, Alex Fratzl, Georg Kosche, Ruchi Sharma, Jair Montford, Marco Cattaneo, Mikaël Croyal, Therese Cronin, Simone Picelli, Alice Grison, Cameron S Cowan, Ákos Kusnyerik, Philipp Anders, Magdalena Renner, Zoltán Zsolt Nagy, Arnold Szabó, Kapil Bharti, Carlo Rivolta, Hendrik P N Scholl, David Bryson, Giuseppe Ciaramella, Botond Roska, Bence György Nature Medicine 2025
Engineering infrared light detection in blind human retina using ultrasensitive human TRPV1 channels Morgan Chevalier, Firas Fadel, Tímea Májer, Dániel Péter Magda, Lili Gerendás, Ferenc Kilin, Zoltán Zsolt Nagy, Arnold Szabó, Botond Roska, Guilherme Testa-Silva Trends Biotechnol. 2025
PCDH15 dual-AAV gene therapy for deafness and blindness in Usher syndrome type 1F models Maryna V Ivanchenko, Daniel M Hathaway, Eric M Mulhall, Kevin Ta Booth, Mantian Wang, Cole W Peters, Alex J Klein, Xinlan Chen, Yaqiao Li, Bence György, David P Corey  J Clin Invest. 2024
Retinal Disorders José-Alain Sahel, Eyal Banin, Jean Bennett, Jacque L Duncan, Botond Roska Cold Spring Harbor Laboratory Press 2024
Optogenetic vision restoration Volker Busskamp, Botond Roska, Jose-Alain Sahel Cold Spring Harb Perspect Med. 2024
Toward Retinal Organoids in High-Throughput Stefan Erich Spirig, Magdalena Renner Cold Spring Harb Perspect Med. 2024
Prevalence Factors Associated With Vision Impairment and Blindness Among Individuals 85 Years and Older in Russia Mukharram M Bikbov, Gyulli M Kazakbaeva, Ellina M Rakhimova, Iuliia A Rusakova, Albina A Fakhretdinova, Azaliia M Tuliakova, Songhomitra Panda-Jonas, Timur R Gilmanshin, Rinat M Zainullin, Natalia I Bolshakova, Kamilia R Safiullina, Ainur V Gizzatov, Ildar P Ponomarev, Dilya F Yakupova, Nail E Baymukhametov, Nikolay A Nikitin, Jost B Jonas JAMA network open 2021